Kiana has a form of Spinal muscular atrophy. Will she get access to a drug that could have amazing effects on her condition?
30 August 2017
While there is no cure for spinal muscular atrophy (SMA), a promising new drug has been approved for use in America.
40% of patients treated with Spinraza showed an improvement in their ‘motor milestones’, such as head control, sitting, ability to kick in supine position, rolling, crawling, standing and walking.
Charities are now petitioning for the drug to become available in the UK.
Latest features from BBC Scotland
-
![]()
'Wild swimming helps me process the grief of losing my son'
The benefits of cold water therapy.
-
![]()
Winter adventures are appealing, but an expert advises caution
Trips in winter require particular knowledge and skills.
-
![]()
The rescuers: Why volunteers risk their lives in mountain emergencies
Landward meets members of the Cairngorm Mountain Rescue Team.
-
![]()
‘Look for the light’ – practical tips to help you through another winter with SAD
Useful advice and tips to combat low moods at this time of year.
-
![]()
How you could be a binge drinker without even knowing
Binge drinking is classed as fewer units than many people may realise.
-
![]()
How chocolate biscuits and drama classes helped one man leave prison behind
The healing power of creativity.
-
![]()
'When people believe in you, it’s life-changing'
Author Graeme Armstrong revisits the man who helped turn his life around.
-
![]()
The 'breath-taking' display of US birds swept on to British soil
Recent storms have brought rare birds to our shores.
-
![]()
Six things we learned about Alan Cumming on Take the Floor (Spoiler: includes accordions)
The actor spoke to Take the Floor's Gary Innes.
-
![]()
How street gangs trap young men in a dangerous cycle of violence
The almost inescapable pull of life in a gang.
-
![]()
Why stylist Gok Wan believes there's no such thing as bad fashion
The fashion expert says we should stop following rules and do what feels right.
-
![]()
Is sending a CV still the right way to apply for a job?
They've been central to job applications for years, but are they worth it?
